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Amy L White Selected Research
Amy L White Research Topics
Disease
2
Mucopolysaccharidosis I (Hurler Syndrome)
01/2020 - 08/2008
1
Rhizomelic Chondrodysplasia Punctata
11/2023
1
Zellweger Syndrome (Zellweger's Syndrome)
11/2023
1
Peroxisomal Disorders (Peroxisomal Disorder)
11/2023
1
Congenital Disorders of Glycosylation
07/2022
1
Neoplasms (Cancer)
01/2022
1
Hematologic Neoplasms (Hematological Malignancy)
01/2022
1
Metabolic Diseases (Metabolic Disease)
01/2021
1
Globoid Cell Leukodystrophy (Krabbe Disease)
01/2020
1
Glycogen Storage Disease Type II (Pompe's Disease)
08/2008
1
Mucopolysaccharidosis VI (Syndrome, Maroteaux-Lamy)
08/2008
1
Gaucher Disease (Gaucher's Disease)
08/2008
1
Inborn Genetic Diseases (Disease, Hereditary)
08/2008
1
Lysosomal Storage Diseases (Lysosomal Storage Disease)
08/2008
1
Mucopolysaccharidosis II (Hunter Syndrome)
08/2008
1
Fabry Disease (Fabry's Disease)
08/2008
Drug/Important Bio-Agent (IBA)
1
Plasmalogens
IBA
11/2023
1
glucosidase I
IBA
07/2022
1
Chimeric Antigen Receptors
IBA
01/2022
1
Neoplasm Antigens (Tumor Antigens)
IBA
01/2022
1
Acute Hepatic Porphyria
IBA
01/2021
1
Galactosylceramidase
IBA
01/2020
1
Psychosine (Galactosylsphingosine)
IBA
01/2020
1
Biomarkers (Surrogate Marker)
IBA
01/2020
1
Enzymes
IBA
01/2020
1
alglucerase
FDA Link
08/2008
Therapy/Procedure
1
Therapeutics
01/2022
1
Enzyme Replacement Therapy
08/2008